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| ID | DOID:350 |
| Name | mastocytosis |
| Definition | |
| Source | DiseaseOntology.org |
| Alt Ids | |
| Path | disease disease of anatomical entity hematopoietic system disease leukocyte disease mastocytosis |
| Molecular Profile | Therapy | Indication/Tumor Type | Response Type | Profile Response Detail |
|---|---|---|---|---|
| KIT D419del | Imatinib | mastocytosis | predicted - sensitive | detail... |
| KIT K509I | Imatinib | mastocytosis | sensitive | detail... |
| Clinical Trial | Phase | Therapies | Title | Recruitment Status | Covered Countries | Other Countries |
|---|---|---|---|---|---|---|
| NCT00814073 | Phase III | Masitinib | A Phase 3 Study to Compare Efficacy and Safety of Masitinib to Placebo in the Treatment of Patients With Smouldering Systemic, Indolent Systemic or Cutaneous Mastocytosis With Handicap | Completed | USA | FRA | 0 |
| NCT04333108 | Phase III | Masitinib | Masitinib in Severe Indolent or Smoldering Systemic Mastocytosis Unresponsive to Optimal Symptomatic Treatment | Unknown status | ROU | POL | NLD | GBR | FRA | DEU | 2 |
| NCT06327685 | Phase I | Avapritinib + Decitabine Avapritinib + Decitabine and Cedazuridine | Avapritinib With Decitabine in Patients With SM-AHN | Recruiting | USA | 0 |
| NCT06915766 | Expanded access | PLX9486 | Expanded Access to Bezuclastinib for Patients With NonAdvanced Systemic Mastocytosis or Advanced Systemic Mastocytosis | Available | USA | 0 |