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| Drug Name | RAG-01 |
| Trade Name | |
| Synonyms | RAG 01|RAG01 |
| Drug Descriptions |
RAG-01 is a small activating RNA targeting CDKN1A (p21), which upregulates CDKN1A (p21) gene expression, potentially resulting in antitumor activity (J Clin Oncol 2025 43: 16_suppl, e16587). |
| DrugClasses | |
| CAS Registry Number | NA |
| NCIT ID | C215089 |
| Therapy Name | Drugs | Efficacy Evidence | Clinical Trials |
|---|---|---|---|
| RAG-01 | RAG-01 | 0 | 1 |