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| Drug Name | PTC124 |
| Trade Name | Ataluren |
| Synonyms | PTC-124|PTC 124 |
| Drug Descriptions |
Ataluren (PTC124) is a non-aminoglycoside compound that potentially increases readthrough of premature termination codons, leading to restoration of protein expression and decreased tumor cell growth (PMID: 36428516). |
| DrugClasses | |
| CAS Registry Number | 775304-57-9 |
| NCIT ID | C169791 |
| Therapy Name | Drugs | Efficacy Evidence | Clinical Trials |
|---|---|---|---|
| Pembrolizumab + PTC124 | PTC124 Pembrolizumab | 0 | 1 |
| PTC124 | PTC124 | 0 | 0 |